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The Platform Vector Gene Therapies Project: Increasing the Efficiency of Adeno-Associated Virus Gene Therapy Clinical Trial Startup

作者:Philip J. Brooks, Elizabeth A. Ottinger, Deanna Portero, Richa Madan Lomash, Asaf Alimardanov, Pramod Terse, Xin Xu, Randy J. Chandler, Janelle Geist Hauserman, Eric Esposito, Carsten G. Bönnemann, Charles P. Venditti, Christopher P. Austin, Anne Pariser, Donald C. Lo, for the NIH PaVe-GT Team, G. Averion, Krishna Balakrishnan, Steven J. Burden, Eggerton Campbell, Catherine Chen, Claire T. Driscoll, Oksana I. Dukhanina, Susan Ferry, Alicia Foley, Lina Li, Irini Manoli, Christopher Mendoza, Julien Oury, Forbes D. Porter, Lili Portilla, Dimah Saade, Oleg A. Shchelochkov, Jennifer L. Sloan, Joshua J. Todd, London Toney, Carol Van Ryzin, Sury Vepa, E. F. Wagner, Amy Wang · 发表于:Human Gene Therapy · 年份:2020 · DOI:10.1089/hum.2020.259 · 被引用次数:34 · 研究领域:Virus-based gene therapy research、CRISPR and Genetic Engineering、CAR-T cell therapy research