Randy J. Chandler

机构：National Human Genome Research Institute · ORCID：0000-0002-6047-5230

发表论文 70 篇 · 总被引 3405 次 · h-index 30

代表论文

• Evaluating the state of the science for adeno-associated virus integration: An integrated perspective (2022 · Molecular Therapy · 被引 206)
• Gene Therapy for Methylmalonic Acidemia: Past, Present, and Future (2019 · Human Gene Therapy · 被引 56)
• Promoterless, Nuclease‐Free Genome Editing Confers a Growth Advantage for Corrected Hepatocytes in Mice With Methylmalonic Acidemia (2020 · Hepatology · 被引 55)
• Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease (2020 · Molecular Therapy · 被引 51)
• Low incidence of hepatocellular carcinoma in mice and cats treated with systemic adeno-associated viral vectors (2020 · Molecular Therapy — Methods & Clinical Development · 被引 49)
• ImmTOR nanoparticles enhance AAV transgene expression after initial and repeat dosing in a mouse model of methylmalonic acidemia (2021 · Molecular Therapy — Methods & Clinical Development · 被引 38)