A. Saveliev

机构：University of Pennsylvania

发表论文 11 篇 · 总被引 364 次 · h-index 6

代表论文

• Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol (2018 · Nature Biotechnology · 被引 126)
• CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX–knockout mice (2019 · Blood · 被引 86)
• A mutation-independent CRISPR-Cas9–mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency (2020 · Science Advances · 被引 66)
• Transcription Mapping and Expression Patterns of Genes in the Major Immediate-Early Region of Kaposi's Sarcoma-Associated Herpesvirus (2002 · Virology · 被引 56)
• The Severity of Retinal Degeneration in Rp1h Gene-Targeted Mice Is Dependent on Genetic Background (2009 · Investigative Ophthalmology & Visual Science · 被引 20)
• Accurate and Rapid Sequence Analysis of Adeno-Associated Virus Plasmids by Illumina Next-Generation Sequencing (2018 · Human Gene Therapy Methods · 被引 8)