Camilo Breton

机构：University of Pennsylvania · ORCID：0000-0001-7482-1918

发表论文 16 篇 · 总被引 705 次 · h-index 11

代表论文

• Integrated vector genomes may contribute to long-term expression in primate liver after AAV administration (2023 · Nature Biotechnology · 被引 136)
• Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol (2018 · Nature Biotechnology · 被引 126)
• CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX–knockout mice (2019 · Blood · 被引 86)
• CRISPR/Cas9 directed to the Ube3a antisense transcript improves Angelman syndrome phenotype in mice (2021 · Journal of Clinical Investigation · 被引 66)
• A mutation-independent CRISPR-Cas9–mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency (2020 · Science Advances · 被引 66)
• ITR-Seq, a next-generation sequencing assay, identifies genome-wide DNA editing sites in vivo following adeno-associated viral vector-mediated genome editing (2020 · BMC Genomics · 被引 60)