Skeletal-muscle-targeted non-viral delivery of full-length DMD mRNA for Duchenne muscular dystrophy

作者：Y W Tian, Yutong Liu, Yuhao Tong, Kristin Huntoon, Liqun Yang, Junfeng Shi, Yifan Ma, Shiyan Dong, Seong Dong Jeong, Andreanne Poppy Estania, You Yi, Kwang Joo Kwak, Yifan Wang, Annette Wu, Jared L. Edwards, Xiaotian Wang, Yen-Tzu Chang, Jianhong Cao, Haitao Zhang, Man Sun, Adam Grippin, Zhaogang Yang, Wenjing Lu, L. James Lee, Eman Bahrani, Hongjia Zhang, Lu Bai, P. H. Nguyen, Wen Jiang, Feng Lan, Betty Y.S. Kim, Andrew S. Lee · 发表于：Nature Biomedical Engineering · 年份：2026 · DOI：10.1038/s41551-026-01689-5 · 被引用次数：1 · 研究领域：Muscle Physiology and Disorders、Extracellular vesicles in disease、interferon and immune responses