In vivo genome editing of human haematopoietic stem cells for treatment of blood disorders using mRNA delivery

作者：Saijuan Xu, Dan Liang, Qiudao Wang, Yan Cheng, Da Xie, Gui Yang, Haokun Zhang, Changrui Feng, Feiyan Zhao, Wendan Ren, Gongrui Sun, Yang Yang, Lin Li, Yongrong Lai, Bin Fu, Yuming Lu, Zi Jun Wang, Yuxuan Wu · 发表于：Nature Biomedical Engineering · 年份：2025 · DOI：10.1038/s41551-025-01480-y · 被引用次数：13 · 研究领域：RNA Interference and Gene Delivery、CRISPR and Genetic Engineering、Virus-based gene therapy research