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AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

作者:Jieyu Qi, Liyan Zhang, Ling Lü, Fangzhi Tan, Cheng Cheng, Yicheng Lu, Wenxiu Dong, Yinyi Zhou, Xiaolong Fu, Lulu Jiang, Chang Tan, Shanzhong Zhang, Sijie Sun, Huaien Song, Maoli Duan, Dingjun Zha, Yu Sun, Xia Gao, Lei Xu, Fan‐Gang Zeng, Renjie Chai · 发表于:Nature Medicine · 年份:2025 · DOI:10.1038/s41591-025-03773-w · 被引用次数:43 · 研究领域:Hearing, Cochlea, Tinnitus, Genetics、RNA regulation and disease、Virus-based gene therapy research