Daratumumab in Relapsed or Refractory Pediatric Immune Thrombocytopenia

作者：Ting Sun, Yunfei Chen, Lei Zhang · 发表于：New England Journal of Medicine · 年份：2025 · DOI：10.1056/nejmc2501527 · 被引用次数：11 · 研究领域：Platelet Disorders and Treatments、Chronic Lymphocytic Leukemia Research、Autoimmune Bullous Skin Diseases

Twenty children with relapsed or refractory immune thrombocytopenia were treated with daratumumab. Most patients had a response, platelet counts increased quickly, and responses were durable in half the patients.