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Long-term lineage commitment in haematopoietic stem cell gene therapy

作者:Andrea Calabria, Giulio Spinozzi, Daniela Cesana, Elena Buscaroli, Fabrizio Benedicenti, Giulia Pais, Francesco Gazzo, Serena Scala, Maria Rosa Lidonnici, Samantha Scaramuzza, Alessandra Albertini, Simona Esposito, Francesca Tucci, Daniele Canarutto, Maryam Omrani, Fabiola De Mattia, Francesca Dionisio, Stefania Giannelli, Sarah Marktel, Francesca Fumagalli, Valeria Calbi, Sabina Cenciarelli, Francesca Ferrua, Bernhard Gentner, Giulio Caravagna, Fabio Ciceri, Luigi Naldini, Giuliana Ferrari, Alessandro Aiuti, Eugenio Montini · 发表于:Nature · 年份:2024 · DOI:10.1038/s41586-024-08250-x · 被引用次数:44 · 研究领域:Prenatal Screening and Diagnostics、CRISPR and Genetic Engineering、Cancer Genomics and Diagnostics