AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial
作者:Jun Lv, Hui Wang, Xiaoting Cheng, Yuxin Chen, Daqi Wang, Longlong Zhang, Qi Cao, Honghai Tang, Shaowei Hu, Kaiyu Gao, Mengzhao Xun, Jinghan Wang, Zijing Wang, Biyun Zhu, Chong Cui, Ziwen Gao, Luo Guo, Sha Yu, Luoying Jiang, Yanbo Yin, Jiajia Zhang, Bing Chen, Wuqing Wang, Renjie Chai, Zheng‐Yi Chen, Huawei Li, Yilai Shu · 发表于:The Lancet · 年份:2024 · DOI:10.1016/s0140-6736(23)02874-x · 被引用次数:342 · 研究领域:Hearing, Cochlea, Tinnitus, Genetics、Virus-based gene therapy research、Hearing Loss and Rehabilitation