P35 Two-year clinical outcomes with fordadistrogene movaparvovec (FM) for Duchenne muscular dystrophy (DMD) and contextualization with external controls

作者：Perry B. Shieh, Russell J. Butterfield, Francesco Muntoni, Eugenio Mercuri, J. Signorovitch, Peter H. Schwartz, H. Li, Michael Binks, Thomas McDonnell, Karen K. Ryan, Marielle Delnomdedieu, Qiujin Shen, Deborah M. Levy, Edward C. Smith · 发表于：Neuromuscular Disorders · 年份：2023 · DOI：10.1016/j.nmd.2023.07.162 · 被引用次数：1 · 研究领域：Muscle Physiology and Disorders