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PK/PD and Bioanalytical Considerations of AAV-Based Gene Therapies: an IQ Consortium Industry Position Paper

作者:Uma Kavita, Kefeng Sun, Manuela Braun, Wibke Lembke, Hardik Mody, John Kamerud, Tong‐Yuan Yang, Inka V. Braun, Xiaodong Fang, Wei Gao, Swati Gupta, Magdalena Hofer, Michael Z. Liao, LiNa Loo, Fraser McBlane, Karelle Ménochet, Kay‐Gunnar Stubenrauch, Vijay Upreti, Adam Vigil, Christopher M. Wiethoff, Cindy Q. Xia, Xu Zhu, Vibha Jawa, Nagendra Chemuturi · 发表于:The AAPS Journal · 年份:2023 · DOI:10.1208/s12248-023-00842-1 · 被引用次数:21 · 研究领域:Virus-based gene therapy research、CRISPR and Genetic Engineering、Viral gastroenteritis research and epidemiology