Elimination of Toxic Microsatellite Repeat Expansion RNA by RNA-Targeting Cas9

作者：Ranjan Batra, David A. Nelles, Elaine Pirie, Steven M. Blue, Ryan J. Marina, Harrison Wang, Isaac A. Chaim, James D. Thomas, Nigel Zhang, Vu Nguyen, Stefan Aigner, Sebastian Markmiller, Guangbin Xia, Kevin D. Corbett, Maurice S. Swanson, G Yeo · 发表于：Cell · 年份：2017 · DOI：10.1016/j.cell.2017.07.010 · 被引用次数：258 · 研究领域：Genetic Neurodegenerative Diseases、CRISPR and Genetic Engineering、RNA Research and Splicing