Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo

作者：Hao Yin, Chun‐Qing Song, J. Robert Dorkin, Lihua Julie Zhu, Yingxiang Li, Qiongqiong Wu, Angela Park, Junghoon Yang, Sneha Suresh, Aizhan Bizhanova, Ankit Gupta, Mehmet Fatih Bolukbasi, Stephen C. Walsh, Roman L. Bogorad, Guangping Gao, Zhiping Weng, Yizhou Dong, Victor Koteliansky, Scot A. Wolfe, Róbert Langer, Wen Xue, Daniel G. Anderson · 发表于：Nature Biotechnology · 年份：2016 · DOI：10.1038/nbt.3471 · 被引用次数：889 · 研究领域：CRISPR and Genetic Engineering、RNA regulation and disease、Virus-based gene therapy research