Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype

作者：Hao Yin, Wen Xue, Sidi Chen, Roman L. Bogorad, Eric Benedetti, Markus Grompe, Victor Koteliansky, Phillip A. Sharp, Tyler Jacks, Daniel G. Anderson · 发表于：Nature Biotechnology · 年份：2014 · DOI：10.1038/nbt.2884 · 被引用次数：967 · 研究领域：CRISPR and Genetic Engineering、Evolution and Genetic Dynamics、Genetics, Aging, and Longevity in Model Organisms