Paula R. Clemens

机构：University of Pittsburgh · ORCID：0000-0002-0652-6703

发表论文 233 篇 · 总被引 15666 次 · h-index 57

代表论文

First-in-human study of epidural spinal cord stimulation in individuals with spinal muscular atrophy (2025 · Nature Medicine · 被引 25)
Adrenal Suppression From Vamorolone and Prednisone in Duchenne Muscular Dystrophy: Results From the Phase 2b Clinical Trial (2024 · The Journal of Clinical Endocrinology & Metabolism · 被引 16)
Safety and efficacy of viltolarsen in ambulatory and nonambulatory males with Duchenne muscular dystrophy (2024 · Scientific Reports · 被引 12)
Efficacy and safety of avalglucosidase alfa in patients with late-onset Pompe disease after 145 weeks of treatment during the COMET trial (2025 · Journal of Neurology · 被引 9)
Mineralocorticoid receptor antagonism of vamorolone: Evidence from LIONHEART and VISION-DMD clinical trials (2025 · Steroids · 被引 8)
Switching Enzyme Replacement Therapy for Late‐Onset Pompe Disease From Alglucosidase Alfa to Cipaglucosidase Alfa Plus Miglustat: Post Hoc Effect Size Analysis of PROPEL (2025 · Muscle & Nerve · 被引 6)