Janet L. Kwiatkowski

机构：Children's Hospital of Philadelphia, Hospital of the University of Pennsylvania, University of Pennsylvania · ORCID：0000-0001-7103-3406

发表论文 277 篇 · 总被引 9467 次 · h-index 50

代表论文

Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial (2024 · The Lancet · 被引 40)
An Update on Lovotibeglogene Autotemcel (Lovo-cel) Clinical Trials for Sickle Cell Disease (SCD) and Analysis of Early Predictors of Response to Lovo-Cel (2024 · Blood · 被引 12)
Impact of HLA alloimmunization in gene-modified autologous stem cell transplant for transfusion-dependent thalassemia (2025 · Blood · 被引 7)
Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel (2025 · Blood Advances · 被引 4)
Durable Clinical Benefits with Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia (2024 · Blood · 被引 4)
Betibeglogene Autotemcel (beti-cel) Gene Addition Therapy Results in Durable Hemoglobin a Production with up to 10 Years of Follow-up with Transfusion-Dependent β-Thalassemia (2024 · Blood · 被引 3)