Julie Douville
ORCID:0000-0001-8783-6676
发表论文 24 篇 · 总被引 1638 次 · h-index 12
代表论文
- Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease (2019 · New England Journal of Medicine · 被引 844)
- ALDH1 as a Functional Marker of Cancer Stem and Progenitor Cells (2008 · Stem Cells and Development · 被引 358)
- An ASO therapy for Angelman syndrome that targets an evolutionarily conserved region at the start of the UBE3A-AS transcript (2023 · Science Translational Medicine · 被引 97)
- Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder (2024 · Nature Medicine · 被引 60)
- The effect of angiotensin receptor neprilysin inhibitor, sacubitril/valsartan, on central nervous system amyloid-β concentrations and clearance in the cynomolgus monkey (2017 · Toxicology and Applied Pharmacology · 被引 45)
- The state-of-the-art of N-of-1 therapies and the IRDiRC N-of-1 development roadmap (2024 · Nature Reviews Drug Discovery · 被引 40)