Curt Mazur

机构：Ionis Pharmaceuticals (United States) · ORCID：0000-0003-3485-9086

发表论文 74 篇 · 总被引 5752 次 · h-index 27

代表论文

• Long pre-mRNA depletion and RNA missplicing contribute to neuronal vulnerability from loss of TDP-43 (2011 · Nature Neuroscience · 被引 1399)
• Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis (2012 · Neuron · 被引 786)
• Divergent roles of ALS-linked proteins FUS/TLS and TDP-43 intersect in processing long pre-mRNAs (2012 · Nature Neuroscience · 被引 766)
• Antisense oligonucleotides extend survival of prion-infected mice (2019 · JCI Insight · 被引 158)
• The atlas of RNase H antisense oligonucleotide distribution and activity in the CNS of rodents and non-human primates following central administration (2020 · Nucleic Acids Research · 被引 129)
• Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging (2019 · JCI Insight · 被引 114)