Irene Gil-Fariña

机构：Knowledge Unlatched (Germany), Gene Bridges (Germany) · ORCID：0009-0000-9822-3170

发表论文 31 篇 · 总被引 910 次 · h-index 13

代表论文

• Evaluating the state of the science for adeno-associated virus integration: An integrated perspective (2022 · Molecular Therapy · 被引 209)
• Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria (2016 · Journal of Hepatology · 被引 144)
• In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model (2017 · Molecular Therapy · 被引 53)
• Therapeutic expression of human clotting factors IX and × following adeno‐associated viral vector‐mediated intrauterine gene transfer in early‐gestation fetal macaques (2018 · The FASEB Journal · 被引 33)
• Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer (2024 · Blood · 被引 27)
• Systematic comparative study of computational methods for T-cell receptor sequencing data analysis (2017 · Briefings in Bioinformatics · 被引 20)