Andrea Frassetto

ORCID：0000-0002-3957-2984

发表论文 83 篇 · 总被引 4056 次 · h-index 24

代表论文

• Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates (2019 · The American Journal of Human Genetics · 被引 168)
• Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia (2020 · Nature Communications · 被引 126)
• Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia (2019 · EBioMedicine · 被引 86)
• Synthetic human ABCB4 mRNA therapy rescues severe liver disease phenotype in a BALB/c.Abcb4 mouse model of PFIC3 (2020 · Journal of Hepatology · 被引 73)
• mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency (2019 · Molecular Therapy · 被引 73)
• mRNA therapy restores euglycemia and prevents liver tumors in murine model of glycogen storage disease (2021 · Nature Communications · 被引 69)