Johannes C.M. van der Loo

机构：Children's Hospital of Philadelphia

发表论文 49 篇 · 总被引 3732 次 · h-index 22

代表论文

• Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant (2017 · New England Journal of Medicine · 被引 776)
• The clinical landscape for AAV gene therapies (2021 · Nature Reviews Drug Discovery · 被引 522)
• A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency (2014 · New England Journal of Medicine · 被引 414)
• Familial pulmonary alveolar proteinosis caused by mutations in CSF2RA (2008 · The Journal of Experimental Medicine · 被引 302)
• Cell Cycle-Related Changes in Repopulating Capacity of Human Mobilized Peripheral Blood CD34+ Cells in Non-Obese Diabetic/Severe Combined Immune-Deficient Mice (1998 · Blood · 被引 290)
• Progress and challenges in viral vector manufacturing (2015 · Human Molecular Genetics · 被引 265)