Russell C. DeKelver

机构：University of California San Diego

发表论文 38 篇 · 总被引 5757 次 · h-index 19

代表论文

In vivo genome editing of the albumin locus as a platform for protein replacement therapy (2015 · Blood · 被引 300)
Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing (2018 · Molecular Therapy · 被引 126)
SRSF2 Is Essential for Hematopoiesis, and Its Myelodysplastic Syndrome-Related Mutations Dysregulate Alternative Pre-mRNA Splicing (2015 · Molecular and Cellular Biology · 被引 99)
Non-viral Delivery of Zinc Finger Nuclease mRNA Enables Highly Efficient In Vivo Genome Editing of Multiple Therapeutic Gene Targets (2019 · Molecular Therapy · 被引 96)
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome (2018 · Molecular Therapy · 被引 85)
SON Protein Regulates GATA-2 through Transcriptional Control of the MicroRNA 23a∼27a∼24-2 Cluster* (2013 · Journal of Biological Chemistry · 被引 42)